Vertex Pharmaceuticals Inc.
Vertex Pharmaceuticals Incorporated is focused on discovering, developing and producing innovative medicines so people with serious diseases can lead better lives. They are researching multiple approaches to treat the underlying causes of sickle cell disease and transfusion-dependent beta thalassemia. Vertex is committed to making a difference for patients who are waiting.
Vertex Pharmaceuticals and CRISPR Therapeutics are researching the use of CRISPR/Cas9 gene editing to develop potential new treatments aimed at the underlying genetic causes of human disease, including transfusion-dependent β-thalassemia and severe sickle cell disease.